Department of Anesthesiology
Author Title Type [ Year(Desc)]
Filters: Keyword is Mutation and Author is Worgall, Stefan  [Clear All Filters]
2004
Crystal RG, Sondhi D, Hackett NR, Kaminsky SM, Worgall S, Stieg P, Souweidane M, Hosain S, Heier L, Ballon D et al..  2004.  Clinical protocol. Administration of a replication-deficient adeno-associated virus gene transfer vector expressing the human CLN2 cDNA to the brain of children with late infantile neuronal ceroid lipofuscinosis.. Hum Gene Ther. 15(11):1131-54.